The U.S. has approved the world’s first medicine employing Crispr technology, a Nobel Prize-winning discovery that promised a powerful new tool for modifying genes to treat disease.
The new treatment, called Casgevy and developed by Vertex Pharmaceuticals and Crispr Therapeutics, was cleared for treatment of people with severe forms of the painful sickle-cell disease.
The landmark decision by the Food and Drug Administration heralds a powerful new kind of medicine, one that turns off or replaces genes to tackle conditions that have long confounded doctors and researchers.
~Wall Street Journal today.
https://freerepublic.com/focus/news/4202267/posts?page=1
FDA approves world’s first CRISPR gene-editing drug for sickle cell disease
washingtonexaminer ^ | 12/8/2023 | by Gabrielle M. Etzel,