Skip to comments.4-year-old who was deemed 'lazy' finds hope in new drug that treats rare disease
Posted on 01/18/2017 7:10:23 AM PST by workerbee
A new drug is offering hope for the family of a little girl whose genetic defect causes mobility issues similar to that of polio and amyotrophic lateral sclerosis (ALS).
Four-year-old Lexi Pacini, of Colorado Springs, was diagnosed with type 2 spinal muscular atrophy (SMA) as a toddler. The rare disease is marked by the absence of a gene that codes protein signals from motor neurons to muscles, and it leads muscles to weaken to the point of atrophy.
She dances the way she knows how, in her walker, Tammy told Childrens Hospital Colorado in the release. She just doesnt give up. She wonders why she cant do certain things, and well tell her, Well, youre just not as strong. You dont have as much muscle. And shell just say, No, I have muscles. Im strong.
(Excerpt) Read more at foxnews.com ...
How can this be? I though the pharma industry was poisoning us, or trying to make us all into autistic robots? </s>
The parents of 13-year old Caitlin Teagart have decided to end her life, saying she can now do nothing but lay on the couch and whine about things being "gay."
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